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ESGCT Congress, 17 - 20 September 2015
THURSDAY 17 SEPTEMBER 2015 17:00-18:00
ESGCT 2015 OPENING: Seppo Ylä-Herttuala Chairs: Seppo Ylä-Herttuala, Nathalie Cartier
Nanoscopy with focused light - Nobel laureate Stefan Hell [FinVector Vision Therapies]
Finlandia-hall 18:00-19:00 19:00-21.00
ESGCT –JSGT: Debate on Germline Editing Chairs: Nathalie Cartier-Lacave, Seppo Ylä-Herttuala,
Panel: Kazuto Kato, Annelien Bredenoord, Robin Lovell-Badge,Bernard Baertschi, Luigi Naldini, Adrian Thrasher Welcome address: Helsinki City Deputy Mayor, Laura Räty
WELCOME RECEPTION POSTER SESSION 1
FRIDAY 18 SEPTEMBER 2015 08:30-10:00
REC
EPTI
ON
PLENARY SESSION 1: Highlights of Clinical Progress I – Common diseases [Oxford Biomedica]
Chairs: Robin Ali, Kyriacos Mitrophanous Finlandia-hall
Inv 0031 Zelig Eshhar, inv 0032 Michel Sadelain OR001 Sabena Sultan OR002 Pierre Cordelier
10:00-10:30 COFFEE BREAK Piazza 10:30-12:30 S2a: Cell and Gene Therapy of Cancer
[Amgen, JSGT] Chairs: Hildegard Büning, Rolf Bjerkvig
INV033 Angelica Loskog INV034 Rolf Bjerkvig INV035 Tomoki Todo
Finlandia-hall OR003 Margherita Norelli OR004 Osvaldo Podhajcer
S2b: Viral vectors I [Bioreliance]
Chairs: Luigi Naldini, Stefan Kochanek INV036 Thierry vandenDriessche
INV037 Andy Baker
Helsinki Hall OR005 Irène Gil Farinas OR006 Yasuhiro Ikeda
OR007 Verena Emmerling
S2c: Cardiovascular Diseases
Chairs: Andy Baker, Petra Korpisalo INV038 Seppo Ylä-Herttuala
INV039 Roger Hajjar
Veranda 1 OR008 Jarkko Hytönen
OR009 Ralf Bauer OR010 Gabor Rubanyi
12:30-14:00 ESGCT Assembly LUNCH Piazza
14:00-15:30 PLENARY SESSION 2: Therapeutic targeting of non-coding RNAs Chairs: Hidde Haisma, Edvard Smith
INV040 Kevin Morris, INV041 Marco Weinberg, INV042 Gioacchino Natoli Finlandia-hall
ESGCT Congress, 17 - 20 September 2015
15:30-16:00 COFFEE BREAK Piazza 16:00-18:00 S3a: Innate Immunity and
Stem Cell Therapy Chairs: Sarah Ferber, Angelica
Loskog [Sangamo, JSGT]
INV043 Niels-Bjarne Woods
INV044 Tani Kenzaburo
Finlandia-hall OR011 Judith Lorant
OR012 Pietro Genovese OR013 Tolga Sutlu
S3b: Epigenetic Regulation and Gene Editing
Chairs: Kevin Morris, Marco Weinberg
[Nature Publishing Group; Supersist]
INV045 Michael Holmes
Helsinki Hall OR014 Carles Calatayud
Aristoy OR015 Diego Balboa Alonso
OR016 William Kelton OR017 Kaihsin Chang OR018 Mikko Turunen OR019 Giulia Schiroli
S3c: Ocular Diseases
Chairs: Arto Urtti, Gabrielle Thumann
[Avalanche Biotechnologies]
INV046 Robin Ali INV047 Alberto Auriccio
INV048 TBC Veranda 2
OR020 Céline Bouquet OR021 Sophia-Martha Kleine
Holthaus
S3d: Vector Safety and Genotoxicity
Chairs: Diana Schenkwein, Fulvio Mavilio
[Biovian]
INV049 Christof von Kalle INV050 Eugenio Montini
Veranda 1
OR022 Stefan Wilkening OR023 Daniela Cesana OR024 Teng Cheong Ha
18:00-19:30 POSTER SESSION 2
SATURDAY 19 SEPTEMBER 2015 8:30-10:00
PLENARY SESSION 3: Highlights of Clinical Progress II – Rare diseases Chairs: Adrian Thrasher, Olivier Danos
[Biogen, Lysogene] INV051 Alain Fischer, INV052 Gabor Veres
OR025 Cécile Bauche OR026 Karen Aiach
Finlandia-hall
10:00-10:30 COFFEE BREAK Piazza 10:30-12:30
S4a: RNA Therapeutics
Chairs:Vincenzo Cerullo, Mikko Turunen
INV053 Thomas Thum
INV054 Nihay Laham-Karam Finlandia-hall
OR027 Ai-Li Shiau OR028 Pia Laitinen
OR029 Jana Miniarikova OR030 Rasmus Bak
S4b: Neural Diseases
Chairs: Nathalie Cartier, Karen Kozarsky
[ReGenX] INV055 Françoise Pujol INV056 Alessandra Biffi
Helsinki Hall OR031 Marc Tardieu OR032 Angela Gritti OR033 Romain Fol
S4c: Blood-related Diseases
Chair: Juan Bueren, Sandeep Soni
[Bluebird Bio, JSGT] INV057 Masafumi Onodera
INV058 Giuliana Ferrari Veranda 2
OR034 Juan Bueren OR035 Lucia Sereni OR036 Nir Shapir
OR037 Tayebeh Soheili
S4d: Muscle and Mesenchyme-related Diseases
Chair: Thierry vandenDriessche, Francesco Muntoni
[AFM] INV059 Fulvio Mavilio
Veranda 1
OR038 Marinee K.L. Chuah OR039 Nicholas Mazarakis
OR040 Daria Wojtal OR041 Ignazio Maggio
OR042 Francesco Saverio Tedesco OR043 Ana Buj Bello
ESGCT Congress, 17 - 20 September 2015
12:30-13:30 LUNCH Piazza
13:30-14:30
PLENARY SESSION 4: Genetic Medicine: Current Challenges and Future Prospects Chairs: Seppo Ylä-Herttuala, Michel Sadelain
[Editas Medicine] INV060 Keith Joung, INV061 Frederic Bushman
Finlandia-hall
14:30-16:30 S5a: Metabolic Diseases and Primary Immune Deficiencies
Chairs: Alessandro Aiuti, Jenni Huusko [GenoSafe, Cellpid]
INV062 Adrian Thrasher
Finlandia-hall OR044 Brian Bigger OR045 Fyodor Urnov
OR046 Raymond Hickey OR047 Yasuhiro Ikeda
OR048 Francesca Santoni de Sio
S5b: Non-viral vectors
Chairs: Samir El-Andaloussi, Zoltan Ivics [Target AMD]
INV063 Edvard Smith INV064 Gabrielle Thumann
Veranda 2 OR049 Deborah Gil OR050 Marta Holstein
OR051 Anthony Delalande
S5c: Oncolytic Vectors and Therapies
Chairs: Len Seymour, Hrvoje Miletic
INV065 Richard Vile INV066 Akseli Hemminki
Helsinki Hall OR052 Vincenzo Cerullo OR053 Gunnel Hallden OR054 Alexander Muik
16:30-17:00 COFFEE BREAK Piazza 17:00-19:00 S6a: Modelling and IPSCells
Chairs: Juan Bueren, Matti
Korhonen INV067 Ian Alexander
INV068 Nathalie Cartier INV069 Tom Moritz
Helsinki Hall OR055 Miriam Hetzel OR056 Serena Scala
S6b: Exosomes and Nanoparticles
Chairs: Edvard Smith, Petri Mäkinen
INV070 Samir El-Andaloussi INV071 Zachary Fitzpatrick
Veranda 2
OR057 Susanne Snoek OR058 Lotta Kilpinen OR059 Chin-Yu Lin
OR060 Marina Radrizzano
S6c: Regulatory Issues
Chairs: Minna Hassinen, Otto Merten [Bluebird Bio]
INV072 Paula Salmikangas INV073 Anne Virginie Eggiman
INV074 TBC Veranda 1
OR061 Aurélie Mahalatchimy OR062 Ursula Jenal
S6d: Vascular Biology and Imaging
Chairs: Johanna Laakkonen, Roger Hajjar
INV075 Kari Alitalo INV076 Juhani Knuuti
INV077 TBC Helsinki Hall
OR063 Pyry Toivanen OR064 Andrea Banfi
20:00- GALA DINNER Restaurant Sipuli
ESGCT Congress, 17 - 20 September 2015
SUNDAY 20 SEPTEMBER 2015 9:00-11:00 S7a: Regenerative Medicine
Chairs: Sarah Ferber, Niels Bjarne-Woods
[Pall Corporation, JSGT] INV078 Kenneth Chien INV079 Katsuto Tamai
Finlandia-hall OR065 Chiara Bonini OR066 Sofiane Hamidi OR067 Petra Korpisalo OR068 Peter Ponsaerts
S7b: Bioprocessing of Cell &Gene Therapy Products
Chairs: Klaus Kühlchke, Hanna Lesch [Eufets]
INV080 Otto Merten INV081 Robert Kotin
Veranda 2 OR069 Matthias Hebben OR070 Hanna Lesch
OR071 Margarida Serra OR072 Lauren Nickolay
S7c: Viral vectors II
Chairs, Kari Airenne, Christof von Kalle [Avalanche Biotechnologies]
INV082 (TBC)
Finlandia-hall OR073 Jessica Harmann OR074 Akiko Makino
OR075 Alexandra Sharland OR076 Araksya Izmiryan OR077 Heikki Turunen
11:00-11:30 COFFEE BREAK Piazza 11:30-13:30
PRESIDENTIAL SYMPOSIUM AWARDS CEREMONY [Généthon]
Chairs: Nathalie Cartier, Seppo Ylä-Herttuala
PRESIDENTIAL CONFERENCE INV083 Malcolm Brenner
INV084 Luigi Naldini (Outstanding Achievement Award) SPONSORED BY HUMAN GENE THERAPY INV085 TBA (Young Investigator Award)
Finlandia-hall
14:00 ESGCT BOARD MEETING