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ESGCT Congress, 17 - 20 September 2015 THURSDAY 17 SEPTEMBER 2015 17:00-18:00 ESGCT 2015 OPENING: Seppo Ylä-Herttuala Chairs: Seppo Ylä-Herttuala, Nathalie Cartier Nanoscopy with focused light - Nobel laureate Stefan Hell [FinVector Vision Therapies] Finlandia-hall 18:00-19:00 19:00-21.00 ESGCT –JSGT: Debate on Germline Editing Chairs: Nathalie Cartier-Lacave, Seppo Ylä-Herttuala, Panel: Kazuto Kato, Annelien Bredenoord, Robin Lovell-Badge,Bernard Baertschi, Luigi Naldini, Adrian Thrasher Welcome address: Helsinki City Deputy Mayor, Laura Räty WELCOME RECEPTION POSTER SESSION 1 FRIDAY 18 SEPTEMBER 2015 08:30-10:00 RECEPTION PLENARY SESSION 1: Highlights of Clinical Progress I – Common diseases [Oxford Biomedica] Chairs: Robin Ali, Kyriacos Mitrophanous Finlandia-hall Inv 0031 Zelig Eshhar, inv 0032 Michel Sadelain OR001 Sabena Sultan OR002 Pierre Cordelier 10:00-10:30 COFFEE BREAK Piazza 10:30-12:30 S2a: Cell and Gene Therapy of Cancer [Amgen, JSGT] Chairs: Hildegard Büning, Rolf Bjerkvig INV033 Angelica Loskog INV034 Rolf Bjerkvig INV035 Tomoki Todo Finlandia-hall OR003 Margherita Norelli OR004 Osvaldo Podhajcer S2b: Viral vectors I [Bioreliance] Chairs: Luigi Naldini, Stefan Kochanek INV036 Thierry vandenDriessche INV037 Andy Baker Helsinki Hall OR005 Irène Gil Farinas OR006 Yasuhiro Ikeda OR007 Verena Emmerling S2c: Cardiovascular Diseases Chairs: Andy Baker, Petra Korpisalo INV038 Seppo Ylä-Herttuala INV039 Roger Hajjar Veranda 1 OR008 Jarkko Hytönen OR009 Ralf Bauer OR010 Gabor Rubanyi 12:30-14:00 ESGCT Assembly LUNCH Piazza 14:00-15:30 PLENARY SESSION 2: Therapeutic targeting of non-coding RNAs Chairs: Hidde Haisma, Edvard Smith INV040 Kevin Morris, INV041 Marco Weinberg, INV042 Gioacchino Natoli Finlandia-hall

ESGCT Congress, 17 - 20 September 2015 THURSDAY 17 SEPTEMBER 2015 Program with selected... · 2015-07-23 · ESGCT Congress, 17 - 20 September 2015 ! THURSDAY 17 SEPTEMBER 2015 17:00-18:00

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ESGCT Congress, 17 - 20 September 2015  

THURSDAY 17 SEPTEMBER 2015 17:00-18:00

ESGCT 2015 OPENING: Seppo Ylä-Herttuala Chairs: Seppo Ylä-Herttuala, Nathalie Cartier

Nanoscopy with focused light - Nobel laureate Stefan Hell [FinVector Vision Therapies]

Finlandia-hall 18:00-19:00 19:00-21.00

ESGCT –JSGT: Debate on Germline Editing Chairs: Nathalie Cartier-Lacave, Seppo Ylä-Herttuala,

Panel: Kazuto Kato, Annelien Bredenoord, Robin Lovell-Badge,Bernard Baertschi, Luigi Naldini, Adrian Thrasher Welcome address: Helsinki City Deputy Mayor, Laura Räty

WELCOME RECEPTION POSTER SESSION 1

FRIDAY 18 SEPTEMBER 2015 08:30-10:00

REC

EPTI

ON

PLENARY SESSION 1: Highlights of Clinical Progress I – Common diseases [Oxford Biomedica]

Chairs: Robin Ali, Kyriacos Mitrophanous Finlandia-hall

Inv 0031 Zelig Eshhar, inv 0032 Michel Sadelain OR001 Sabena Sultan OR002 Pierre Cordelier

10:00-10:30 COFFEE BREAK Piazza 10:30-12:30 S2a: Cell and Gene Therapy of Cancer

[Amgen, JSGT] Chairs: Hildegard Büning, Rolf Bjerkvig

INV033 Angelica Loskog INV034 Rolf Bjerkvig INV035 Tomoki Todo

Finlandia-hall OR003 Margherita Norelli OR004 Osvaldo Podhajcer

S2b: Viral vectors I [Bioreliance]

Chairs: Luigi Naldini, Stefan Kochanek INV036 Thierry vandenDriessche

INV037 Andy Baker

Helsinki Hall OR005 Irène Gil Farinas OR006 Yasuhiro Ikeda

OR007 Verena Emmerling

S2c: Cardiovascular Diseases

Chairs: Andy Baker, Petra Korpisalo INV038 Seppo Ylä-Herttuala

INV039 Roger Hajjar

Veranda 1 OR008 Jarkko Hytönen

OR009 Ralf Bauer OR010 Gabor Rubanyi

12:30-14:00 ESGCT Assembly LUNCH Piazza

14:00-15:30 PLENARY SESSION 2: Therapeutic targeting of non-coding RNAs Chairs: Hidde Haisma, Edvard Smith

INV040 Kevin Morris, INV041 Marco Weinberg, INV042 Gioacchino Natoli Finlandia-hall

ESGCT Congress, 17 - 20 September 2015  

15:30-16:00 COFFEE BREAK Piazza 16:00-18:00 S3a: Innate Immunity and

Stem Cell Therapy Chairs: Sarah Ferber, Angelica

Loskog [Sangamo, JSGT]

INV043 Niels-Bjarne Woods

INV044 Tani Kenzaburo

Finlandia-hall OR011 Judith Lorant

OR012 Pietro Genovese OR013 Tolga Sutlu

S3b: Epigenetic Regulation and Gene Editing

Chairs: Kevin Morris, Marco Weinberg

[Nature Publishing Group; Supersist]

INV045 Michael Holmes

Helsinki Hall OR014 Carles Calatayud

Aristoy OR015 Diego Balboa Alonso

OR016 William Kelton OR017 Kaihsin Chang OR018 Mikko Turunen OR019 Giulia Schiroli

S3c: Ocular Diseases

Chairs: Arto Urtti, Gabrielle Thumann

[Avalanche Biotechnologies]

INV046 Robin Ali INV047 Alberto Auriccio

INV048 TBC Veranda 2

OR020 Céline Bouquet OR021 Sophia-Martha Kleine

Holthaus

S3d: Vector Safety and Genotoxicity

Chairs: Diana Schenkwein, Fulvio Mavilio

[Biovian]

INV049 Christof von Kalle INV050 Eugenio Montini

Veranda 1

OR022 Stefan Wilkening OR023 Daniela Cesana OR024 Teng Cheong Ha

18:00-19:30 POSTER SESSION 2  

SATURDAY 19 SEPTEMBER 2015 8:30-10:00

PLENARY SESSION 3: Highlights of Clinical Progress II – Rare diseases Chairs: Adrian Thrasher, Olivier Danos

[Biogen, Lysogene] INV051 Alain Fischer, INV052 Gabor Veres

OR025 Cécile Bauche OR026 Karen Aiach

Finlandia-hall

10:00-10:30 COFFEE BREAK Piazza 10:30-12:30  

 

   

S4a: RNA Therapeutics

Chairs:Vincenzo Cerullo, Mikko Turunen

INV053 Thomas Thum

INV054 Nihay Laham-Karam Finlandia-hall

OR027 Ai-Li Shiau OR028 Pia Laitinen

OR029 Jana Miniarikova OR030 Rasmus Bak

S4b: Neural Diseases

Chairs: Nathalie Cartier, Karen Kozarsky

[ReGenX] INV055 Françoise Pujol INV056 Alessandra Biffi

Helsinki Hall OR031 Marc Tardieu OR032 Angela Gritti OR033 Romain Fol

S4c: Blood-related Diseases

Chair: Juan Bueren, Sandeep Soni

[Bluebird Bio, JSGT] INV057 Masafumi Onodera

INV058 Giuliana Ferrari Veranda 2

OR034 Juan Bueren OR035 Lucia Sereni OR036 Nir Shapir

OR037 Tayebeh Soheili

S4d: Muscle and Mesenchyme-related Diseases

Chair: Thierry vandenDriessche, Francesco Muntoni

[AFM] INV059 Fulvio Mavilio

Veranda 1

OR038 Marinee K.L. Chuah OR039 Nicholas Mazarakis

OR040 Daria Wojtal OR041 Ignazio Maggio

OR042 Francesco Saverio Tedesco OR043 Ana Buj Bello

ESGCT Congress, 17 - 20 September 2015  

12:30-13:30 LUNCH Piazza  

13:30-14:30

PLENARY SESSION 4: Genetic Medicine: Current Challenges and Future Prospects Chairs: Seppo Ylä-Herttuala, Michel Sadelain

[Editas Medicine] INV060 Keith Joung, INV061 Frederic Bushman

Finlandia-hall

14:30-16:30 S5a: Metabolic Diseases and Primary Immune Deficiencies

Chairs: Alessandro Aiuti, Jenni Huusko [GenoSafe, Cellpid]

INV062 Adrian Thrasher

Finlandia-hall OR044 Brian Bigger OR045 Fyodor Urnov

OR046 Raymond Hickey OR047 Yasuhiro Ikeda

OR048 Francesca Santoni de Sio

S5b: Non-viral vectors

Chairs: Samir El-Andaloussi, Zoltan Ivics [Target AMD]

INV063 Edvard Smith INV064 Gabrielle Thumann

Veranda 2 OR049 Deborah Gil OR050 Marta Holstein

OR051 Anthony Delalande

S5c: Oncolytic Vectors and Therapies

Chairs: Len Seymour, Hrvoje Miletic

INV065 Richard Vile INV066 Akseli Hemminki

Helsinki Hall OR052 Vincenzo Cerullo OR053 Gunnel Hallden OR054 Alexander Muik

16:30-17:00 COFFEE BREAK Piazza 17:00-19:00 S6a: Modelling and IPSCells

Chairs: Juan Bueren, Matti

Korhonen INV067 Ian Alexander

INV068 Nathalie Cartier INV069 Tom Moritz

Helsinki Hall OR055 Miriam Hetzel OR056 Serena Scala

S6b: Exosomes and Nanoparticles

Chairs: Edvard Smith, Petri Mäkinen

INV070 Samir El-Andaloussi INV071 Zachary Fitzpatrick

Veranda 2

OR057 Susanne Snoek OR058 Lotta Kilpinen OR059 Chin-Yu Lin

OR060 Marina Radrizzano

S6c: Regulatory Issues

Chairs: Minna Hassinen, Otto Merten [Bluebird Bio]

INV072 Paula Salmikangas INV073 Anne Virginie Eggiman

INV074 TBC Veranda 1

OR061 Aurélie Mahalatchimy OR062 Ursula Jenal

S6d: Vascular Biology and Imaging

Chairs: Johanna Laakkonen, Roger Hajjar

INV075 Kari Alitalo INV076 Juhani Knuuti

INV077 TBC Helsinki Hall

OR063 Pyry Toivanen OR064 Andrea Banfi

20:00- GALA DINNER Restaurant Sipuli

 

 

 

 

 

 

 

 

ESGCT Congress, 17 - 20 September 2015  

 

 

 

 

 

 

 

 

 

SUNDAY 20 SEPTEMBER 2015 9:00-11:00 S7a: Regenerative Medicine

Chairs: Sarah Ferber, Niels Bjarne-Woods

[Pall Corporation, JSGT] INV078 Kenneth Chien INV079 Katsuto Tamai

Finlandia-hall OR065 Chiara Bonini OR066 Sofiane Hamidi OR067 Petra Korpisalo OR068 Peter Ponsaerts

S7b: Bioprocessing of Cell &Gene Therapy Products

Chairs: Klaus Kühlchke, Hanna Lesch [Eufets]

INV080 Otto Merten INV081 Robert Kotin

Veranda 2 OR069 Matthias Hebben OR070 Hanna Lesch

OR071 Margarida Serra OR072 Lauren Nickolay

S7c: Viral vectors II

Chairs, Kari Airenne, Christof von Kalle [Avalanche Biotechnologies]

INV082 (TBC)

Finlandia-hall OR073 Jessica Harmann OR074 Akiko Makino

OR075 Alexandra Sharland OR076 Araksya Izmiryan OR077 Heikki Turunen

11:00-11:30 COFFEE BREAK Piazza 11:30-13:30

PRESIDENTIAL SYMPOSIUM AWARDS CEREMONY [Généthon]

Chairs: Nathalie Cartier, Seppo Ylä-Herttuala

PRESIDENTIAL CONFERENCE INV083 Malcolm Brenner

INV084 Luigi Naldini (Outstanding Achievement Award) SPONSORED BY HUMAN GENE THERAPY INV085 TBA (Young Investigator Award)

Finlandia-hall

14:00 ESGCT BOARD MEETING